An investigational gene therapy showed sustained clinical efficacy for children born with ADA-SCID. In a study of 62 children, overall survival after treatment was 100% and event-free survival was 95% ...
Children born without a working immune system due to a rare genetic disorder called Artemis-deficient severe combined immunodeficiency (Artemis-deficient SCID) may be able to lead normal lives thanks ...
There are several types of SCID, based on which gene defect is involved; mutations in the IL2RG gene on the X chromosome cause X-linked SCID or SCID-X1, which primarily affects infant boys. The ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback